Browsing ODA Open Digital Archive by Author "Wallace, Sean Ciaran"

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    • Type 1 spinal muscular atrophy treated with nusinersen in Norway, a five-year follow-up 

      Wik-Klokk, Merete; Rasmussen, Magnhild; Ørstavik, Kristin; Zetterberg, Henrik; Hagen, Milada; Holtebekk, Elisabeth; Ramm-Pettersen, Anette; Wallace, Sean Ciaran (Peer reviewed; Journal article, 2024)
      Background: New treatments for 5q spinal muscular atrophy (SMA) have led to changes in the disease phenotype. Questions about long-term efficacy, however, persist. We present the results from five-year follow-up of the ...